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1 Ergebnisse
1
First-in-human invivo genome editing via AAV-zinc-finger nu..:
Prada, Carlos
;
Burton, Barbara
;
Lau, Heather
...
qt0qq0z34p. , 2022
Link:
https://escholarship.org/uc/item/0qq0z34p
RT Journal T1
First-in-human invivo genome editing via AAV-zinc-finger nucleases for mucopolysaccharidosis I/II and hemophilia B
UL https://suche.suub.uni-bremen.de/peid=base-ftcdlib:oai:escholarship.org:ark:_13030_qt0qq0z34p&Exemplar=1&LAN=DE A1 Prada, Carlos A1 Burton, Barbara A1 Lau, Heather A1 Kessler, Craig A1 Cao, Liching A1 Falaleeva, Marina A1 Villegas, Andres A1 Zeitler, Jennifer A1 Meyer, Kathleen A1 Miller, Weston A1 Wong Po Foo, Cheryl A1 Vaidya, Sagar A1 Swenson, Wendy A1 Shiue, Lisa A1 Rouy, Didier A1 Muenzer, Joseph A1 Harmatz, Paul PB eScholarship, University of California YR 2022 K1 MPS I K1 MPS II K1 first-in-human K1 hemophilia K1 in vivo genome editing K1 mucopolysaccharidosis K1 zinc-finger nuclease K1 Humans K1 Zinc Finger Nucleases JF qt0qq0z34p LK http://dx.doi.org/https://escholarship.org/uc/item/0qq0z34p DO https://escholarship.org/uc/item/0qq0z34p SF ELIB - SuUB Bremen
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