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1 Ergebnisse
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Safety outcomes and patients' preferences for home-based in..:
Antonio Toscano
;
Olimpia Musumeci
;
Michele Sacchini
...
https://doi.org/10.1186/s13023-023-02919-8. , 2023
Link:
https://doi.org/10.1186/s13023-023-02919-8
RT Journal T1
Safety outcomes and patients' preferences for home-based intravenous enzyme replacement therapy (ERT) in pompe disease and mucopolysaccharidosis type I (MPS I) disorder: COVID-19 and beyond
UL https://suche.suub.uni-bremen.de/peid=base-ftdoajarticles:oai:doaj.org_article:0a5becd85d924dc1b04b318ba6f147bc&Exemplar=1&LAN=DE A1 Antonio Toscano A1 Olimpia Musumeci A1 Michele Sacchini A1 Sabrina Ravaglia A1 Gabriele Siciliano A1 Agata Fiumara A1 Elena Verrecchia A1 Melania Maione A1 Jennifer Gentile A1 Rita Fischetto A1 Grazia Crescimanno A1 Roberta Taurisano A1 Annalisa Sechi A1 Serena Gasperini A1 Vittoria Cianci A1 Lorenzo Maggi A1 Rossella Parini A1 Antonino Lupica A1 Maurizio Scarpa PB BMC YR 2023 K1 Enzyme replacement therapy K1 Pompe disease K1 Home therapy K1 Mucopolysaccharidosis K1 Treatment adherence K1 Safety K1 Medicine K1 R JF https://doi.org/10.1186/s13023-023-02919-8 LK http://dx.doi.org/https://doi.org/10.1186/s13023-023-02919-8 DO https://doi.org/10.1186/s13023-023-02919-8 SF ELIB - SuUB Bremen
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