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Longitudinal evaluation of SMN levels as biomarker for spin..:

Tiziano, FD ; Lomastro, R ; Abiusi, E...
https://discovery.ucl.ac.uk/id/eprint/10068409/7/Baranello_Longitudinal%20evaluation%20of%20SMN%20levels%20as%20biomarker%20for%20spinal%20muscular%20atrophy.%20Results%20of%20a%20phase%20IIb%20double-blind%20study%20of%20salbutamol_AAM.pdf.  , 2018