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Novel therapies for mucopolysaccharidosis type III:

Seker Yilmaz, B ; Davison, J ; Jones, SA.
https://discovery.ucl.ac.uk/id/eprint/10110949/1/Baruteau_J%20of%20Inher%20Metab%20Disea%20-%202020%20-%20Seker%20Yilmaz%20-%20Novel%20therapies%20for%20mucopolysaccharidosis%20type%20III.pdf.  , 2021