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Safety and efficacy of an engineered hepatotropic AAV gene ..:

Baruteau, J ; Cunningham, SC ; Yilmaz, BS...
https://discovery.ucl.ac.uk/id/eprint/10136674/1/Baruteau_Safety%20and%20efficacy%20of%20an%20engineered%20hepatotropic%20AAV%20gene%20therapy%20for%20ornithine%20transcarbamylase%20deficiency%20in%20cynomolgus%20monkeys_VoR.pdf.  , 2021