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Intracranial delivery of AAV9 gene therapy partially preven..:

White, KA ; Nelvagal, HR ; Poole, TA...
https://discovery.ucl.ac.uk/id/eprint/10144987/1/Intracranial%20delivery%20of%20AAV9%20gene%20therapy%20partially%20prevents%20retinal%20degeneration%20and%20visual%20deficits%20in%20CLN6-Batten%20diseas.pdf.  , 2021