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1 Ergebnisse
1
Transiently expressed CRISPR/Cas9 induces wild-type dystrop..:
Pini, Veronica
;
Mariot, Virginie
;
Dumonceaux, Julie
...
https://discovery.ucl.ac.uk/id/eprint/10145227/1/Pini_s41598-022-07671-w.pdf. , 2022
Link:
https://discovery.ucl.ac.uk/id/eprint/10145227/1/Pini_..
RT Journal T1
Transiently expressed CRISPR/Cas9 induces wild-type dystrophin in vitro in DMD patient myoblasts carrying duplications
UL https://suche.suub.uni-bremen.de/peid=base-ftucl:oai:eprints.ucl.ac.uk.OAI2:10145227&Exemplar=1&LAN=DE A1 Pini, Veronica A1 Mariot, Virginie A1 Dumonceaux, Julie A1 Counsell, John A1 O'Neill, Helen C A1 Farmer, Sarah A1 Conti, Francesco A1 Muntoni, Francesco PB Springer Science and Business Media LLC YR 2022 K1 Cell delivery K1 Genetic transduction K1 Targeted gene repair K1 Transfection JF https://discovery.ucl.ac.uk/id/eprint/10145227/1/Pini_s41598-022-07671-w.pdf LK http://dx.doi.org/https://discovery.ucl.ac.uk/id/eprint/10145227/1/Pini_s41598-022-07671-w.pdf DO https://discovery.ucl.ac.uk/id/eprint/10145227/1/Pini_s41598-022-07671-w.pdf SF ELIB - SuUB Bremen
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