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Clinical Trial Readiness for Spinal Muscular Atrophy: Exper..:

Tizzano, Eduardo F ; Christie-Brown, Vanessa ; Baranello, Giovanni...
https://discovery.ucl.ac.uk/id/eprint/10164623/2/Baranello_Tizzano.E%20ScotoM.%20Clinical%20trial%20workshop.revised%20version%201%20-%20VCB.pdf.  , 2022