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Clinical applications of gene therapy for rare diseases: A ..:

Papaioannou, Ioannis ; Owen, James S ; Yáñez-Muñoz, Rafael J
https://discovery.ucl.ac.uk/id/eprint/10170190/1/Clinical%20applications%20of%20gene%20therapy%20for%20rare%20diseases%20%20A%20review.pdf.  , 2023