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1 Ergebnisse
1
Indirect Comparison of Lenadogene Nolparvovec Gene Therapy ..:
Carelli, Valerio
;
Newman, Nancy J
;
Yu-Wai-Man, Patrick
...
https://discovery.ucl.ac.uk/id/eprint/10182177/1/Indirect%20Comparison%20of%20Lenadogene%20Nolparvovec%20Gene%20Therapy%20Versus%20Natural%20History%20in%20Patients%20with%20Leber%20Hereditary%20Optic%20Ne.pdf. , 2023
Link:
https://discovery.ucl.ac.uk/id/eprint/10182177/1/Indir..
RT Journal T1
Indirect Comparison of Lenadogene Nolparvovec Gene Therapy Versus Natural History in Patients with Leber Hereditary Optic Neuropathy Carrying the m.11778G>A MT-ND4 Mutation
UL https://suche.suub.uni-bremen.de/peid=base-ftucl:oai:eprints.ucl.ac.uk.OAI2:10182177&Exemplar=1&LAN=DE A1 Carelli, Valerio A1 Newman, Nancy J A1 Yu-Wai-Man, Patrick A1 Biousse, Valerie A1 Moster, Mark L A1 Subramanian, Prem S A1 Vignal-Clermont, Catherine A1 Wang, An-Guor A1 Donahue, Sean P A1 Leroy, Bart P A1 Sergott, Robert C A1 Klopstock, Thomas A1 Sadun, Alfredo A A1 Fernandez, Gema Rebolleda A1 Chwalisz, Bart K A1 Banik, Rudrani A1 Girmens, Jean Francois A1 La Morgia, Chiara A1 DeBusk, Adam A A1 Jurkute, Neringa A1 Priglinger, Claudia A1 Karanjia, Rustum A1 Josse, Constant A1 Salzmann, Julie A1 Montestruc, Francois A1 Roux, Michel A1 Taiel, Magali A1 Sahel, Jose-Alain A1 Group, The Lhon Study PB SPRINGER INT PUBL AG YR 2023 JF https://discovery.ucl.ac.uk/id/eprint/10182177/1/Indirect%20Comparison%20of%20Lenadogene%20Nolparvovec%20Gene%20Therapy%20Versus%20Natural%20History%20in%20Patients%20with%20Leber%20Hereditary%20Optic%20Ne.pdf LK http://dx.doi.org/https://discovery.ucl.ac.uk/id/eprint/10182177/1/Indirect%20Comparison%20of%20Lenadogene%20Nolparvovec%20Gene%20Therapy%20Versus%20Natural%20History%20in%20Patients%20with%20Leber%20Hereditary%20Optic%20Ne.pdf DO https://discovery.ucl.ac.uk/id/eprint/10182177/1/Indirect%20Comparison%20of%20Lenadogene%20Nolparvovec%20Gene%20Therapy%20Versus%20Natural%20History%20in%20Patients%20with%20Leber%20Hereditary%20Optic%20Ne.pdf SF ELIB - SuUB Bremen
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