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Codon-Optimized RPGR Improves Stability and Efficacy of AAV..:

Fischer, M. Dominik ; McClements, Michelle E ; Martinez-Fernandez de la Camara, Cristina...
Fischer , M D , McClements , M E , Martinez-Fernandez de la Camara , C , Bellingrath , J S , Dauletbekov , D , Ramsden , S C , Hickey , D G , Barnard , A R & MacLaren , R E 2017 , ' Codon-Optimized RPGR Improves Stability and Efficacy of AAV8 Gene Therapy in Two Mouse Models of X-Linked Retinitis Pigmentosa ' , Molecular Therapy . https://doi.org/10.1016/j.ymthe.2017.05.005.  , 2017