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Single AAV-mediated CRISPR-Nme2Cas9 efficiently reduces mut..:

Wen, Jinkun ; Cao, Tianqi ; Wu, Jinni...
Wen , J , Cao , T , Wu , J , Chen , Y , Zhi , S , Huang , Y , Zhen , P , Wu , G , Aagaard , L , Zhong , J , Liang , P & Huang , J 2022 , ' Single AAV-mediated CRISPR-Nme2Cas9 efficiently reduces mutant hTTR expression in a transgenic mouse model of transthyretin amyloidosis ' , Molecular Therapy , vol. 30 , no. 1 , pp. 164-174 . https://doi.org/10.1016/j.ymthe.2021.05.010.  , 2022