Merkliste 
 1 Ergebnisse 
 
1

Safety and early efficacy outcomes for lentiviral fibroblas..:

Liu, Li ; Guy, Alyson ; Petrova, Anastasia...
Lwin, S. M., Syed, F., Di, W.-L., Kadiyirire, T., Liu, L., Guy, A., Petrova, A., Abdul-Wahab, A., Reid, F., Phillips, R., Elstad, M., Georgiadis, C., Aristodemou, S., Lovell, P. A., McMillan, J. R., Mee, J., Miskinyte, S., Titeux, M., Ozoemena, L., … McGrath, J. A. (2019). Safety and early efficacy outcomes for lentiviral fibroblast gene therapy in recessive dystrophic epidermolysis bullosa. JCI Insight,4 (11), pp. 1-20.  , 2019