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Isogenic GAA-KO Murine Muscle Cell Lines Mimicking Severe P..:

Aguilar González, Araceli ; González Correa, Juan Elías ; Barriocanal Casado, Eliana...
Aguilar-González, A. [et al.]. Isogenic GAA-KO Murine Muscle Cell Lines Mimicking Severe Pompe Mutations as Preclinical Models for the Screening of Potential Gene Therapy Strategies. Int. J. Mol. Sci. 2022, 23, 6298. [https://doi.org/10.3390/ijms23116298].  , 2022