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Expanded access program with Nusinersen in SMA type I in It..:
Messina, Sonia
;
Pane, Marika
;
Sansone, Valeria
...
Neuromuscular Disorders. 27 (2017) 12 - p. 1084-1086 , 2017
Link:
https://doi.org/10.1016/j.nmd.2017.09.006
RT Journal T1
Expanded access program with Nusinersen in SMA type I in Italy: Strengths and pitfalls of a successful experience
UL https://suche.suub.uni-bremen.de/peid=cr-10.1016_j.nmd.2017.09.006&Exemplar=1&LAN=DE A1 Messina, Sonia A1 Pane, Marika A1 Sansone, Valeria A1 Bruno, Claudio A1 Catteruccia, Michela A1 Vita, Giuseppe A1 Palermo, Concetta A1 Albamonte, Emilio A1 Pedemonte, Marina A1 Bertini, Enrico A1 Binetti, Luca A1 Mercuri, Eugenio A1 Lauro, Daniela A1 Pallara, Anita A1 Spinoglio, Simona A1 Solinas, Maria Letizia A1 Zappa, Grazia A1 Penno, Francesca A1 Ponzanelli, Cristina A1 Casiraghi, Jacopo A1 Villanova, Marcello A1 Tiziano, Danilo A1 Mandelli, Anna A1 Mastella, Chiara A1 Fontana, Alberto A1 Ambrosini, Anna A1 Leone, Daniela A1 de Sanctis, Roberto A1 Forcina, Nicola A1 Piastra, Marco PB Elsevier BV YR 2017 SN 0960-8966 JF Neuromuscular Disorders VO 27 IS 12 SP 1084 OP 1086 LK http://dx.doi.org/https://doi.org/10.1016/j.nmd.2017.09.006 DO https://doi.org/10.1016/j.nmd.2017.09.006 SF ELIB - SuUB Bremen
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