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1 Ergebnisse
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AAV8 gene therapy reverses cardiac pathology and prevents e..:
Chang, Joshua C.
;
Ryan, Molly R.
;
Stark, Marie C.
...
Molecular Therapy - Methods & Clinical Development. 32 (2024) 1 - p. 101193 , 2024
Link:
https://doi.org/10.1016/j.omtm.2024.101193
RT Journal T1
AAV8 gene therapy reverses cardiac pathology and prevents early mortality in a mouse model of Friedreich's ataxia
UL https://suche.suub.uni-bremen.de/peid=cr-10.1016_j.omtm.2024.101193&Exemplar=1&LAN=DE A1 Chang, Joshua C. A1 Ryan, Molly R. A1 Stark, Marie C. A1 Liu, Su A1 Purushothaman, Pravinkumar A1 Bolan, Fria A1 Johnson, Caitlin A. A1 Champe, Mark A1 Meng, Hui A1 Lawlor, Michael W. A1 Halawani, Sarah A1 Ngaba, Lucie V. A1 Lynch, David R. A1 Davis, Crystal A1 Gonzalo-Gil, Elena A1 Lutz, Cathleen A1 Urbinati, Fabrizia A1 Medicherla, Bala A1 Fonck, Carlos PB Elsevier BV YR 2024 SN 2329-0501 JF Molecular Therapy - Methods & Clinical Development VO 32 IS 1 SP 101193 LK http://dx.doi.org/https://doi.org/10.1016/j.omtm.2024.101193 DO https://doi.org/10.1016/j.omtm.2024.101193 SF ELIB - SuUB Bremen
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