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1 Ergebnisse
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A GLB1 transgene with enhanced therapeutic potential for th..:
Crippa, Stefania
;
Alberti, Gaia
;
Passerini, Laura
...
Molecular Therapy - Methods & Clinical Development. 32 (2024) 3 - p. 101313 , 2024
Link:
https://doi.org/10.1016/j.omtm.2024.101313
RT Journal T1
A GLB1 transgene with enhanced therapeutic potential for the preclinical development of ex-vivo gene therapy to treat mucopolysaccharidosis type IVB
UL https://suche.suub.uni-bremen.de/peid=cr-10.1016_j.omtm.2024.101313&Exemplar=1&LAN=DE A1 Crippa, Stefania A1 Alberti, Gaia A1 Passerini, Laura A1 Savoia, Evelyn Oliva A1 Mancino, Marilena A1 De Ponti, Giada A1 Santi, Ludovica A1 Berti, Margherita A1 Testa, Marialuisa A1 Hernandez, Raisa Jofra A1 Quaranta, Pamela A1 Ceriotti, Selene A1 Visigalli, Ilaria A1 Morrone, Amelia A1 Paoli, Antonella A1 Forni, Claudia A1 Scala, Serena A1 Degano, Massimo A1 Staiano, Leopoldo A1 Gregori, Silvia A1 Aiuti, Alessandro A1 Bernardo, Maria Ester PB Elsevier BV YR 2024 SN 2329-0501 JF Molecular Therapy - Methods & Clinical Development VO 32 IS 3 SP 101313 LK http://dx.doi.org/https://doi.org/10.1016/j.omtm.2024.101313 DO https://doi.org/10.1016/j.omtm.2024.101313 SF ELIB - SuUB Bremen
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