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A translationally optimized AAV-UGT1A1 vector drives safe a..:
Ronzitti, Giuseppe
;
Bortolussi, Giulia
;
van Dijk, Remco
...
Molecular Therapy - Methods & Clinical Development. 3 (2016) - p. 16049 , 2016
Link:
https://doi.org/10.1038/mtm.2016.49
RT Journal T1
A translationally optimized AAV-UGT1A1 vector drives safe and long-lasting correction of Crigler-Najjar syndrome
UL https://suche.suub.uni-bremen.de/peid=cr-10.1038_mtm.2016.49&Exemplar=1&LAN=DE A1 Ronzitti, Giuseppe A1 Bortolussi, Giulia A1 van Dijk, Remco A1 Collaud, Fanny A1 Charles, Severine A1 Leborgne, Christian A1 Vidal, Patrice A1 Martin, Samia A1 Gjata, Bernard A1 Sola, Marcelo Simon A1 van Wittenberghe, Laetitia A1 Vignaud, Alban A1 Veron, Philippe A1 Bosma, Piter J A1 Muro, Andres F A1 Mingozzi, Federico PB Elsevier BV YR 2016 SN 2329-0501 JF Molecular Therapy - Methods & Clinical Development VO 3 SP 16049 LK http://dx.doi.org/https://doi.org/10.1038/mtm.2016.49 DO https://doi.org/10.1038/mtm.2016.49 SF ELIB - SuUB Bremen
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