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1 Ergebnisse
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Safety outcomes and patients' preferences for home-based in..:
Toscano, Antonio
;
Musumeci, Olimpia
;
Sacchini, Michele
...
Orphanet Journal of Rare Diseases. 18 (2023) 1 - p. , 2023
Link:
https://doi.org/10.1186/s13023-023-02919-8
RT Journal T1
Safety outcomes and patients' preferences for home-based intravenous enzyme replacement therapy (ERT) in pompe disease and mucopolysaccharidosis type I (MPS I) disorder: COVID-19 and beyond
UL https://suche.suub.uni-bremen.de/peid=cr-10.1186_s13023-023-02919-8&Exemplar=1&LAN=DE A1 Toscano, Antonio A1 Musumeci, Olimpia A1 Sacchini, Michele A1 Ravaglia, Sabrina A1 Siciliano, Gabriele A1 Fiumara, Agata A1 Verrecchia, Elena A1 Maione, Melania A1 Gentile, Jennifer A1 Fischetto, Rita A1 Crescimanno, Grazia A1 Taurisano, Roberta A1 Sechi, Annalisa A1 Gasperini, Serena A1 Cianci, Vittoria A1 Maggi, Lorenzo A1 Parini, Rossella A1 Lupica, Antonino A1 Scarpa, Maurizio PB Springer Science and Business Media LLC YR 2023 SN 1750-1172 JF Orphanet Journal of Rare Diseases VO 18 IS 1 LK http://dx.doi.org/https://doi.org/10.1186/s13023-023-02919-8 DO https://doi.org/10.1186/s13023-023-02919-8 SF ELIB - SuUB Bremen
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